Disease ProgramResearch Project CodesProject PhaseStatus
Paroxysmal Nocturnal HemoglobinuriaCB101DevelopmentScale-up for IND-Enabling GLP Studies
Retinal Gene TherapyCB201DiscoveryIn Vivo Testing
Neuromyelitis OpticaCB301DiscoveryIn Vitro Research
Myasthenia GravisCB401DiscoveryIn Vitro Research
Renal DiseaseCB501Early DiscoveryIn Vitro Research
CancerCB601Early DiscoveryIn Vitro Research
Prodromal SchizophreniaCB701Early DiscoveryIn Vitro Research
Alzheimer's diseaseCB801Early DiscoveryIn Vitro Research
Amyotrophic Lateral SclerosisCB901Early DiscoveryIn Vitro Research

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